DEC 05, 2018 03:53 PM PST

Promising Results From Early Trials of Gene Therapy for Sickle Cell Anemia

WRITTEN BY: Carmen Leitch

At the recent annual meeting of the American Society of Hematology, researchers reported that very early clinical trials of a gene therapy for sickle cell anemia (SCA) were successful. In two patients, scientists used a modified virus to insert normal fetal hemoglobin genes into the blood stem cells of SCA patients. The 35- and 25-year-old patients’ symptoms were reversed.

"One year after treatment of our first patient, and six months after treatment of our second patient, both have seen a remarkable improvement in the quality of life due to remarkable reduction in disease symptoms," said Punam Malik, professor in the department of pediatrics at University of Cincinnati and the chief investigator of the study. "This includes near elimination of chronic pain and sickling events and improved anemia,” she added.

Source: Cincinnati Children's

About the Author
  • Experienced research scientist and technical expert with authorships on 28 peer-reviewed publications, traveler to over 60 countries, published photographer and internationally-exhibited painter, volunteer trained in disaster-response, CPR and DV counseling.
You May Also Like
OCT 26, 2018
Videos
OCT 26, 2018
Making water out of thin air
The Water Abundance XPRIZE is a two-year competition aimed at encouraging scientists, engineers, and dreamers alike to invent solutions to the global water...
OCT 31, 2018
Space & Astronomy
OCT 31, 2018
Do You Have What it Takes to be an Astronaut?
Have you ever wanted to become an astronaut? If yes, then you’re not alone. Being able to experience zero gravity is a mutual interest among individu...
NOV 07, 2018
Chemistry & Physics
NOV 07, 2018
Why Are Fruit Flies Attracted to Rotting Fruit Smell?
Fruit flies are the staple pests in the kitchen during summer. As much as these unwelcomed guests enjoy sucking up sugary juice, they are actually more att...
NOV 13, 2018
Technology
NOV 13, 2018
Here's Why Hydrogen-Powered Cars Haven't Become Mainstream
The automobile industry today is still dominated by gasoline-powered vehicles, but electric cars like those from Tesla are gaining a lot of traction in the...
NOV 22, 2018
Videos
NOV 22, 2018
The science of gratitude
On a day like Thanksgiving, it is easy to remember all that we are thankful for. But for a while now scientists have been trying to crack the code behind t...
NOV 26, 2018
Health & Medicine
NOV 26, 2018
The Fight Bite
  Human bite wounds are a common source of polymicrobial infections accounting for many emergency room visits. One bacteria, Eikenella corrodens, ...
Loading Comments...