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Adeno-associated Virus
Adeno-associated virus (AAV) are small viruses from the parvovirus family, with a genome of single-stranded DNA. They are vectors that are most frequently used viral vectors for gene therapy. They mostly infect humans, but can also infect other members of the primate family.
JUN 13, 2023 | 10:00 AM
Achieving consistent AAV quantification with the QuantStudio Absolute Q AutoRun dPCR Suite Accurate quantification of AAV vectors is crucial for quality control and timely decision-making du...
MAY 16, 2023 | 5:30 AM
Spinal muscular atrophy (SMA) is a devastating neuromuscular disease caused by mutations in the SMN1 gene that reduce survival motor neuron (SMN) protein expression. Despite progress in the...
APR 05, 2023 | 8:30 AM
The field of gene therapy has enabled the treatment and potential cures for serious, monogenetic diseases. This form of advanced therapy relies on the delivery of the “correct” c...
SEP 29, 2022 | 8:00 AM
Date: September 29, 2022 Time: 8:00am (PDT), 11:00am (EDT), 5:00pm (CEST) Adeno-associated virus (AAV) is one of the most widely used delivery vehicles in gene therapy. To ensure the safety...
SEP 12, 2019 | 10:00 AM
DATE: September 12, 2019TIME: 10:00am PDT, 1:00pm EDT...
OCT 03, 2018 | 10:30 AM
There have been an increasing number of successful human gene therapy clinical trials, and in particular gene delivery vehicles or vectors based on the adeno-associated virus (AAV) have enabl...
MAY 13, 2015 | 5:00 AM
The implementation of Next Generation Sequencing (NGS) technology in the clinical laboratory has allowed for large-scale panel testing of many genes simultaneously at a reduced cost and turn-...
AUG 21, 2014 | 8:45 AM
Gene therapy for two forms of inherited retinal degeneration have met promising safety and efficacy endpoints in early stage clinical trials. These approaches made use of a replication defect...